Disease or Translational Resources

In this section you will have the opportunity to explore information regarding:
Patient registries,
Natural history,
Patients’ information as organizations, toolkits for patients, new-born screening programs, undiagnosed diseases programs (UDPs), EU planned cross-border treatment
Target Patient Value Profile
Databases/Tools (ODDG)
Networks
Biobanks
Biomarkers (Development, guidelines, validation, qualification, genomic, cancer, pain therapeutics)

  1. Showing 83 results for:
  2. Research and Drug Development
  3. Disease or Translational Resources
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Biomarker Validation

Published by Research Advocacy Network

BiomarkerBiomarker ValidationCancer DiseaseDrug Development ToolPreclinicalResearch and Drug Development

This is a review about biomarkers definition and the components of validity. It examines the methods by which biomarkers are validated and consider some examples of cancer biomarkers in use today. It concludes with information about situations where advocates might find this information useful.

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ERNs: a key EU infrastructure to partner for research activities, the why and the how

Published by

European Reference NetworkIndustry collaborationRare DiseaseResearch and Drug Development

The resource explains that European Reference Networks (ERNs) are a major EU healthcare and research infrastructure that bring together clinical expertise, data and specialised resources across Europe to tackle rare and complex diseases and are valuable partners for collaborative research activities. It emphasises the untapped potential of ERNs to engage with the pharmaceutical and biotech sectors, advocating for greater awareness and public–private partnerships to accelerate rare disease research and development and benefit patients

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What can the conect4children Stichting (c4c-S) do for ERNs

Published by

C4CClinical Research NetworkEuropean Reference NetworkNetworkOrphan DrugpaediatricRare DiseaseResearch and Drug Development

conect4children Stichting (c4c-S) is a non-profit, pan-European organisation that supports paediatric clinical research by providing expert advice and trial support services, including feasibility assessments and site identification, for ERNs and other stakeholders. Building on a successful public–private partnership, it mobilises a large network of experts and research-ready sites to improve the efficiency and quality of paediatric trials across Europe.

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