Research and Drug Development

What are the main bottlenecks for advanced therapies for reaching patients?

How do I identify and validate the right disease target?

What are the main mechanisms and tools to search a hit compound?

How do I validate a small molecule lead compound?

How do I optimise a lead compound?

How do I create the formulation and scalability of a lead compound?

How do I choose the right disease model?

How do I develop my biomarker strategy?.

Why is the Natural History so important in rare diseases?

What are the main challenges to develop repurposed drugs?