A neutral comparison of statistical methods for analyzing longitudinally measured ordinal outcomes in rare diseases

Published by Wiley

Clinical Trial Design Research and Drug Development

Peer reviewed journal article on a neutral comparison of statistical methods for longitudinal ordinal outcomes

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How to Analyze Continuous and Discrete Repeated Measures in Small-Sample Cross-Over Trials?

Clinical Trial Design Research and Drug Development

Peer reviewed journal article on a neutral comparison of statistical methods for longitudinal count data and binary data

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Statistical recommendations for count, binary, and ordinal data in rare disease cross-over trials

Published by Springer

Clinical Trial Design Research and Drug Development

Peer reviewed journal article on statistical recommendations for longitudinal cross-over studies in rare disease research

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Learning video project overview

Published by EBStatMax team

Clinical Trial Design Research and Drug Development

Learning Video on the EBStatMax Project Overview

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Learning video statistical recommendations

Published by EBStatMax team

Clinical Trial Design Research and Drug Development

Learning Video on the EBStatMax statistical recommendations

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Learning video educational materials

Published by EBStatMax team

Clinical Trial Design Research and Drug Development

Learning Video on educational materials

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Learning video Rare Disease Analyser

Published by EBStatMax team

Clinical Trial Design Research and Drug Development

Learning Video on the Rare Disease Analyser

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Rare Disease Analyser

Published by Konstantin Emil Thiel (EBStatMax)

Clinical Trial Design Research and Drug Development

Source code of the Rare Disease Analyser, the webapp that implements statistical methods for rare diseases

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Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook

Published by IRDiRC

Database or Tool Research and Drug Development

This review describes IRDiRC Guidebook to facilitate drug development for rare diseases by organizing available tools into a standardized framework.

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Biomarker Validation

Published by Research Advocacy Network

Biomarker Biomarker Validation Cancer Disease Drug Development Tool Preclinical Research and Drug Development

This is a review about biomarkers definition and the components of validity. It examines the methods by which biomarkers are validated and consider some examples of cancer biomarkers in use today. It concludes with information about situations where advocates might find this information useful.

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The Innovation Management Toolbox was originally developed through funding from the EJP RD project, which received funding from the European Union’s Horizon 2020 research and innovation programme under grant agreement No. 825575. The continued development and maintenance of the Toolbox are now supported by the ERDERA partnership, funded under the European Union’s Horizon Europe Research & Innovation programme, grant agreement No. 101156595.

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