Development of new effective therapies for rare diseases

Published by European Commission (EC)

GrantRare Disease

This topic aims at supporting activities that are enabling or contributing to one or several expected impacts of destination 3 “Tackling diseases and reducing disease burden”. To that end, proposals under this topic should aim for delivering results that are directed, tailored towards and contributing to some of the following expected outcomes:

Researchers and developers make the best use of the state-of-the-art knowledge and resources for a fast and effective development of new therapies for rare diseases.
Researchers and developers increase the development success rate of therapies for rare diseases by employing robust preclinical models, methods, technologies, validated biomarkers, reliable patient reported outcomes and/or innovative clinical trials designs.
Developers and regulators move faster towards market approval of new therapies for rare diseases (with currently no approved treatment option) due to an increased number of interventions successfully tested in late stages of clinical development.
Healthcare professionals and people living with a rare disease get access to new therapeutic interventions and/or orphan medicinal products.

View this resource Bookmark this resource

Research Grant for Rett Syndrome

Published by International Rett Syndrome Foundation

GrantRett Syndrome

IRSF believes that research into a variety of Rett and Rett-related topics is necessary to create treatments and eventual cures for every individual living with Rett syndrome. We proudly invest in such research at every stage: from basic science that can change the way we think about MeCP2 to clinical research that directly impacts potential treatments. We also help connect Rett researchers with external funding opportunities.

View this resource Bookmark this resource

CBRC (Comprehensive Biomedical Research Centre): a maximum of £50,000 per award can be applied for using a standard UCLB application form.
Applications for CBRC funded awards require approval by the CBRC Advisory Board.
HEIF (Higher Education Innovation Fund):
applications under £25,000 per award can be applied for using a standard UCLB application form and will be approved internally by UCLB.
Applications exceeding £25,000 will be submitted to the Office of the Vice Provost for Enterprise for approval.
• J&J (Johnson & Johnson) POC: Awards of up to £75,000 are available on a call by call basis.
Preliminary abstracts can be submitted to UCLB and forwarded to J&J. If the abstract is approved, the PI will be invited to submit a full application to the UCLB/J&J committee for final selection.
• MIMIT (Manchester Integrating Medicine &
Innovative Technology): Open to applications on a
case by case call only. Applications can be made to
MIMIT using a dedicated MIMIT application form.
• Moorfields Fund: The Moorfields Fund is open to
applications of up to £50,000 for projects relating to
ophthalmology. Applications over £25,000 require
external independent approval by a dedicated
selection committee.
• UCLB Fund: A UCLB controlled fund of up to
£100,000 per annum. This award is approved and
managed internally by UCLB.

View this resource Bookmark this resource